Prion Disease Treatment: New Advances in Gene Editing

April 7, 2025

Prion disease treatment is at the forefront of groundbreaking therapeutic research aimed at tackling some of the most challenging neurological disorders.These rare diseases, including Creutzfeldt-Jakob disease and fatal familial insomnia, arise from the misfolding of proteins in the brain, leading to devastating cognitive impairments and, ultimately, death.
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